A new paper published in Gene Therapy raises serious concerns about the effectiveness of gene therapy for Duchenne muscular ...

Bluebird Bio and Xcellbio have entered into an agreement to support the commercialization of sickle cell gene therapy ...

Giulio Cossu, MD, University of Manchester, discusses barriers to gene therapy research and development.

Director, Paediatrics, Jaslok Hospital & Research Centre explains how stem cell therapy and regenerative medicine have the ...

For the first time, two U.S. teenagers with sickle cell disease will be able to go swimming on their spring break, thanks to SCD treatments.

For cell and gene therapy, a consistent supply of quality starting material is vital that is maintained throughout the ...

The backstory: Sickle cell anemia is caused by misshapen red blood ... s often out of reach for patients of color. This new gene therapy eliminates the need for a donor and offers a safer, more ...

"If you have sickle cell anemia and you're prone to crisis ... including revolutionary gene-editing therapy, Casgevy, and blood group genotyping to reduce the risk of adverse reactions to blood ...

Patients with MF and anemia had higher median annual all-cause healthcare resource utilization including inpatient admissions, outpatient visits, and emergency department visits compared to patients ...

21-year old Sebastien Beauzile becomes the first person in New York to be cured of sickle cell anemia (Screenshot: Northwell Health/YouTube) ...

This month, 21-year-old Sebastien Beauzile became the first man in New York history to be cured of sickle cell anemia, a genetic blood disorder, thanks to a new form of gene therapy. “ ...