For the first time, two U.S. teenagers with sickle cell disease will be able to go swimming on their spring break, thanks to ...

SNUG01 is a first-in-class targeted gene therapy that’s designed to increase the levels of TRIM72, a protein with ...

Sickle cell disease is the most common inherited haemoglobinopathy in Tanzania, with 11 000– 14 000 children born with the ...

For cell and gene therapy, a consistent supply of quality starting material is vital that is maintained throughout the ...

Kelsi Victorian, 30, has been in and out of the hospital her whole life dealing with a disease that affects millions in the world.

A sickle cell gene therapy treatment has allowed a Long Island man to turn a chapter in his life, with doctors declaring him ...

Sickle cell disease commonly affects people of African and Caribbean backgrounds and can be life-threatening but campaigners ...

Medical history has recently been made in a New York City hospital. This month, 21-year-old Sebastien Beauzile became the ...

Sebastien Beauzile, 21, is the first New Yorker to have received the breakthrough Lyfgenia treatment, according to the New ...

Gene therapy, which promises a possible cure for rare diseases like sickle cell, is losing early investors to higher-reward ...

Sebastien Beauzile lived with the chronic pain of sickle cell anemia. Now, thanks to a groundbreaking genetic treatment, he is the first person in New York to be cured of the disease.

A 21-year-old man has become the first person in New York—and one of the first in the world—to be cured of sickle cell anemia. A novel form of gene therapy enabled the man to receive a life-changing ...