FDA-approved treatments for spinal muscular atrophy differ in their mechanisms of action, safety profiles, and administration ...

Most adolescents and adults with SMA have normal sensory nerve function, even those with long-lasting disease, a study finds.

Hirayama disease is a rare neurological disorder primarily affecting young males. This condition poses diagnostic challenges ...

Intrathecal treatment with a vector-based gene therapy was associated with a greater improvement in motor function at 52 weeks compared with sham in patients aged 2 to 18 years with spinal muscular ...

Novartis has announced positive results from a late-stage programme of its experimental gene replacement therapy in patients with the rare neuromuscular disease spinal muscular atrophy (SMA). The ...

Nearly six years ago, the Food and Drug Administration approved Zolgensma, a Novartis gene therapy for the fatal neuron-wasting disease spinal muscular atrophy. It heralded a new era of genetic ...

In 2022, two children with spinal muscular atrophy died of acute liver failure within weeks of taking onasemnogene abeparvovec (Zolgensma).

The long-awaited and much-anticipated sequel to Rob Reiner's classic 1984 'rockumentary' This Is Spinal Tap is set to open in US cinemas on September 12. The date was revealed as the first short ...

“Spinal Tap II: The End Continues,” a sequel to the 1984 music mockumentary “This Is Spinal Tap,” will rock and roll into theaters this fall. Bleecker Street has acquired U.S. rights to ...

Augmenting rehabilitation robotics with spinal cord neuromodulation: A proof of concept. Science Robotics , 2025; 10 (100) DOI: 10.1126/scirobotics.adn5564 Cite This Page : ...

The long-awaited This Is Spinal Tap sequel is set to hit theaters this fall, and the metal greats are returning with a new set of amps that — believe it or not — go past 11. Spinal Tap II ...