For example, 3D SKMOs derived from patients with DMD have modelled TGFβ-driven fibrosis and muscle contraction failure, providing a platform for optimising exon-skipping therapies. 66 Furthermore, ...

New data from Biogen reveals higher Spinraza doses may enhance motor function in SMA patients. Read more here.

Panelists discuss how spinal muscular atrophy (SMA) treatment will evolve over the next 5 years, likely incorporating ...

BiogenBIIB said Wednesday its experimental treatment helped children with a devastating muscle-wasting disease even after they received an approved gene therapy from NovartisNVS.The company already ...

In a Phase I study, previously treated pediatric SMA patients exhibited reductions in a marker of neurodegeneration after salanersen treatment.

Researchers are exploring how spinal cord stimulation could treat spinal muscular atrophy (SMA) in the future.

Living with SMA isn't just about survival, says columnist. There's also the emotional weight of preparing for the next crisis ...