NEW YORK – Novartis on Wednesday said it plans to submit marketing applications with regulatory agencies for OAV101 IT (onasemnogene abeparvovec), the company's intrathecal gene therapy for spinal ...

The STEER study showed significant motor function improvement in children with SMA using intrathecal onasemnogene abeparvovec. The primary efficacy endpoint was met with a 2.39-point improvement ...

Six years ago, the FDA approved Novartis’ Zolgensma as the first gene therapy for children under two years of age with spinal muscular atrophy. Wednesday, the company reported late-stage data from an ...

WACO — A former high school athletic trainer has been sentenced to seven years in federal prison for the possession of child pornography. According to the U.S. Department of Justice ...

Disease-modifying therapies (DMTs) may help lower the risk of children’s bone fractures among young patients with spinal muscular atrophy (SMA), a study by U.S. researchers suggests. “Drug therapy led ...

The participants in the survey were individuals with neuromuscular diseases, including the following conditions associated with gait disorder: amyotrophic lateral sclerosis, spinal muscular atrophy, ...

Showing his big heart and the immense affection he has for Mexicans, American singer Drake Bell visits a Mexican child in the hospital with Spinal Muscular Atrophy Type 1, seeking support for an ...

In a landmark development, Genrobotics has unveiled India's first robotic-assisted Paediatric Gait Trainer, known as the G-Gaiter Paediatric, to help children with mobility challenges. The innovative ...

The ATLAS2030 exoskeleton is a pediatric device that enables gait rehabilitation for children ... In CP, the damage in the child's Central Nervous System (CNS) shows a different symptomatology than ...