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Some doctors told him he'd live with the disease forever, but Khaled Alsheebani never stopped believing treatments would advance one day.
A Falmouth teen, Jayden Wilsey, is the first to receive gene therapy to treat sickle cell at Boston Children's Hospital.
New gene therapy improves the life of 18-year-old with Sickle Cell Disease which affects 5,000 New Jersey residents living ...
Without the Sickle Cell Data Collection program, we will see greater burdens and higher costs for both families and health ...
Beam reports breakthrough results from BEAM-101's early-stage trial for severe sickle cell disease. Read more here.
Victoria Gray is the first person in the world to receive CRISPR, a gene-editing therapy for sickle cell disease created by ...
Vertex Pharma's £1.65 million ($2.05 million) gene-editing therapy for sickle cell disease (SCD), Casgevy, has been given the green light for use by the NHS in England under a managed access ...
Two Italian women in their twenties on Tuesday received pioneering gene therapy for rare hereditary blood diseases in Pavia ...
Vascarta Receives FDA Orphan Drug Designation for Vasceptor® in the Treatment of Sickle Cell Disease
Orphan Drug Designation is awarded to therapies intended to treat rare diseases that affect fewer than 200,000 people in the ...
A renowned Harvard hematologist, Maureen Okam Achebe, has called for the institutionalisation of continuous newborn screening ...
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