New data from Biogen reveals higher Spinraza doses may enhance motor function in SMA patients. Read more here.

Researchers are exploring how spinal cord stimulation could treat spinal muscular atrophy (SMA) in the future.

For example, 3D SKMOs derived from patients with DMD have modelled TGFβ-driven fibrosis and muscle contraction failure, providing a platform for optimising exon-skipping therapies. 66 Furthermore, ...

Living with SMA isn't just about survival, says columnist. There's also the emotional weight of preparing for the next crisis ...

Today, the FDA approved the first tablet formulation of risdiplam (Evrysdi) for patients with spinal muscular atrophy (SMA) who are at least 2 years of age and weigh more than 44 lbs, according to ...

Symptoms Of Spinal Muscular Atrophy Symptoms of SMA can vary widely depending on the specific type and the age of onset. The most prevalent form of SMA, Type 1, typically has symptoms within the ...

Spinal muscular atrophy (SMA) causes progressive muscular atrophy, weakness, and bulbar dysfunction. It can lead to death, particularly in patients with a homozygous deletion of exon 7 or exons 7 ...

Biohaven's spinal muscular atrophy drug fails to meet study goal. By Mariam E Sunny. November 25, 2024 7:06 PM UTC Updated November 25, 2024 Companies; Biohaven Ltd. Follow. Biogen ...

Health Apta. Spinal Muscular Atrophy Treatment And Management Cost, Guidelines And Other Things To Know. Posted: October 2, 2024 | Last updated: October 2, 2024 ...

Prevalence Of Spinal Muscular Atrophy. Rare diseases affect a small percentage of the population. Despite their rarity, the World Health Organization (WHO) estimates that there are over 7,000 ...

6 Spinal muscular atrophy. Spinal Muscular Atrophy (SMA) is an autosomal recessive neurodegenerative disorder. It is characterized by the loss of lower alpha motor neurons, progressive muscle weakness ...