Despite significant advancements in spinal muscular atrophy (SMA) management, unmet needs persist, especially for patients ...

Evidence suggests inbreeding heightens the risk of birth defects and developmental delays, such as learning and speech ...

Those with spinal muscular atrophy can get emotional support by building an SMA support system that includes SMA communities ...

A case report in Japan shows Spinraza helped a boy with SMA type 0 sit without support for a short time at age 2 and stand ...