After a patient died following a high dose of Neurogene’s Rett syndrome gene therapy candidate, the biotech is sharing ...

The FDA said it has issued its first official green light for a blood test to help diagnose Alzheimer’s disease, adding that ...

BioMarin has followed through on its shift to external innovation, inking a deal to buy Inozyme for $270 million to add a ...

After more than two decades as a Big Pharma cancer leader, Nicholas Botwood is swinging into the biotech world as the new ...

WASHINGTON, D.C.—FDA Commissioner Martin Makary, M.D., offered more details into the agency’s recently announced plans to ...

Rocket Pharmaceuticals has shared early data from three patients that tie its gene therapy for an inherited heart disease to ...

Pathos AI has secured $365 million in a series D raise as the artificial-intelligence-powered biotech looks to fund trials of ...

Despite securing a much-needed $5 million lifeline from an equity offering this week, HCW Biologics is continuing to warn ...

Eli Lilly is further expanding its RNA medicine strategy by tapping South Korea’s Rznomics for a $1.3 billion biobucks deal ...

After publishing early clinical results of its ultrasound-activated brain tumor therapy this year, Alpheus Medical has raised ...

The Garden State is looking to grow into the next big biotech hub. | The Garden State is looking to grow into the next big ...

Biohaven is giving investors whiplash. Forty-eight hours after saying its filing was on track, the biopharma revealed the FDA ...