Spinal muscular atrophy (SMA) is a rare genetic disorder in which the onset of progressive neurodegeneration begins before birth, owing to loss of the protein SMN. Drugs such as risdiplam ...

Spinal muscular atrophy (SMA) is a group of genetic disorders that causes a loss of motor nerve cells and muscle atrophy. There are five types of SMA relating to age of onset and symptom severity.

Since 2016, the FDA has approved three disease-modifying treatments for spinal muscular atrophy, with several ...

Considering taking supplements to treat spinal muscular atrophy? Below is a list of common natural remedies used to treat or reduce the symptoms of spinal muscular atrophy. Follow the links to ...

Opens in a new tab or window How does one time surgery for scoliosis in children with pediatric spinal muscular atrophy get a maximum benefit without impeding growth? Dr. Ashley E. Webb of the ...